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Biomaterials. 2023 Feb;293:121959. doi: 10.1016/j.biomaterials.2022.121959. Epub 2022 Dec 13. PMID: 36527789; PMCID: PMC9868115.
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Sun J, Roy S*. Gene-based therapies for neurodegenerative diseases. Nat Neurosci. 2021 Mar;24(3):297-311. doi: 10.1038/s41593-020-00778-1. Epub 2021 Feb 1. PMID: 33526943; PMCID: PMC8394447.
https://pubmed.ncbi.nlm.nih.gov/33526943/
Saha et al. (SCGE consortium). The NIH Somatic Cell Genome Editing program.
Nature, April 2021: https://www.nature.com/articles/s41586-021-03191-1
https://pubmed.ncbi.nlm.nih.gov/30604771/
Efficient in vivo neuronal genome editing in the mouse brain using nanocapsules containing CRISPR-Cas9 ribonucleoproteins. Metzger JM, Wang Y, Neuman SS, Snow KJ, Murray SA, Lutz CM, Bondarenko V, Felton J, Gimse K, Xie R, Li D, Zhao Y, Flowers MT, Simmons HA, Roy, S, Saha K,
Levine JE, Emborg ME, Gong S.
Biomaterials. 2023 Feb;293:121959. doi: 10.1016/j.biomaterials.2022.121959. Epub 2022 Dec 13. PMID: 36527789; PMCID: PMC9868115.
Review:
Sun J, Roy S*. Gene-based therapies for neurodegenerative diseases. Nat Neurosci. 2021 Mar;24(3):297-311. doi: 10.1038/s41593-020-00778-1. Epub 2021 Feb 1. PMID: 33526943; PMCID: PMC8394447.
https://pubmed.ncbi.nlm.nih.gov/33526943/
Saha et al. (SCGE consortium). The NIH Somatic Cell Genome Editing program.
Nature, April 2021: https://www.nature.com/articles/s41586-021-03191-1